The Official Website of the Acid Maltase Deficiency Association

It is difficult to say what is impossible for the dreams of yesterday are the hopes of today and the reality of tomorrow. - Robert H. Goddard


The AMDA Webinar Program facilitates the exchange of information between the Pompe patient community and professionals that have expertise in the field.

Spark Therapeutics Gene Therapy Research Webinar

Posted on: October 22, 2018 - Filed under

Spark Therapeutics Gene Therapy Research Webinar

Download an audio only version

Other Webinars

Design and Performance of Clinical Trials: An Overview

The contribution of the IPA survey to our understanding of the natural course of Pompe disease

Needle Core Muscle Biopsy

NMR imaging and spectroscopic techniques for diagnosis, follow up and evaluation of Pompe Disease

Respiratory Muscle Strength Training in Pompe Disease

BMN-701:Potentially More Effective Treatment Option for Pompe

Diaphragm Delivery of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase

Autophagy and It’s Role In Pompe Disease

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